20. Adrenoleukodystrophy Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 71 / Drugs : 100 - (DrugBank : 29) / Drug target genes : 22 - Drug target pathways : 125
| Other names | ALD;Childhood cerebral ALD;CCALD;Adolescent cerebral ALD;AdoCALD;AdolCALD;Adrenomyeloneuropathy;AMN;Adult cerebral ALD;ACALD; | ||
|---|---|---|---|
| Disease group | Metabolic diseases | ||
|
Domestic patients
Med expenses recipients, FY2024 (corrected) (in Japanese) |
260 patients Age distribution
|
||
| Clinical research form (in Japanese) MHLW Intractable Diseases, FY2026 (in Japanese) | Overview, diagnostic criteria, etc. (pdf), Clinical research form (pdf) | ||
| Specific pediatric chronic diseases, Japan (in Japanese) | 8-7-104. Adrenoleukodystrophy | ||
| Sub-diseases (Clinical research forms may not be available for all sub-diseases.) | - | ||
