PTC124

( DrugBank: - / KEGG DRUG: - )


4 diseases
IDDisease name (Link within this page)Number of trials
19Lysosomal storage disease2
113Muscular dystrophy53
IDDisease name (Link within this page)Number of trials
246Methylmalonic acidemia5
299Cystic fibrosis50

19. Lysosomal storage disease


Clinical trials : 899Drugs : 684 - (DrugBank : 99) / Drug target genes : 51 - Drug target pathways : 182 
No.TrialIDDate_
enrollment
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registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
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agemin
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PhaseCountries

113. Muscular dystrophy


Clinical trials : 646Drugs : 471 - (DrugBank : 105) / Drug target genes : 59 - Drug target pathways : 170 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

246. Methylmalonic acidemia


Clinical trials : 23Drugs : 31 - (DrugBank : 8) / Drug target genes : 17 - Drug target pathways : 23 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

299. Cystic fibrosis


Clinical trials : 1,695Drugs : 1,527 - (DrugBank : 268) / Drug target genes : 111 - Drug target pathways : 174 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries