Stem cell transplant

( DrugBank: - / KEGG DRUG: - )


7 diseases
IDDisease name (Link within this page)Number of trials
19Lysosomal storage disease22
20Adrenoleukodystrophy9
60Aplastic anemia80
65Primary immunodeficiency50
IDDisease name (Link within this page)Number of trials
96Crohn disease12
164Oculocutaneous albinism7
284Diamond-Blackfan anemia14

19. Lysosomal storage disease


Clinical trials : 990Drugs : 584 - (DrugBank : 126) / Drug target genes : 62 - Drug target pathways : 192 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
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gender
Target_
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PhaseCountries

20. Adrenoleukodystrophy


Clinical trials : 68Drugs : 74 - (DrugBank : 32) / Drug target genes : 25 - Drug target pathways : 131 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

60. Aplastic anemia


Clinical trials : 305Drugs : 328 - (DrugBank : 91) / Drug target genes : 60 - Drug target pathways : 183 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

65. Primary immunodeficiency


Clinical trials : 798Drugs : 585 - (DrugBank : 118) / Drug target genes : 100 - Drug target pathways : 216 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

96. Crohn disease


Clinical trials : 2,737Drugs : 1,197 - (DrugBank : 240) / Drug target genes : 182 - Drug target pathways : 221 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

164. Oculocutaneous albinism


Clinical trials : 16Drugs : 44 - (DrugBank : 27) / Drug target genes : 30 - Drug target pathways : 137 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

284. Diamond-Blackfan anemia


Clinical trials : 39Drugs : 95 - (DrugBank : 35) / Drug target genes : 34 - Drug target pathways : 131 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries