Sapropterin

( DrugBank: Sapropterin / KEGG DRUG: Sapropterin dihydrochloride, Sapropterin )


3 diseases
IDDisease name (Link within this page)Number of trials
240Phenylketonuria65

86. Pulmonary arterial hypertension


Clinical trials : 1,288Drugs : 565 - (DrugBank : 126) / Drug target genes : 81 - Drug target pathways : 191 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

124. Cerebral autosomal dominant arteriopathy with subcortical infarcts and leukoencephalopathy


Clinical trials : 17Drugs : 19 - (DrugBank : 9) / Drug target genes : 6 - Drug target pathways : 24 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

240. Phenylketonuria


Clinical trials : 173Drugs : 95 - (DrugBank : 13) / Drug target gene : 1 - Drug target pathways : 3 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries