Sapropterin

( DrugBank: Sapropterin / KEGG DRUG: Sapropterin dihydrochloride, Sapropterin )


3 diseases
IDDisease name (Link within this page)Number of trials
240Phenylketonuria65

86. Pulmonary arterial hypertension


Clinical trials : 1,348 / Drugs : 828 - (DrugBank : 133) / Drug target genes : 82 - Drug target pathways : 197 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

124. Cerebral autosomal dominant arteriopathy with subcortical infarcts and leukoencephalopathy


Clinical trials : 19 / Drugs : 24 - (DrugBank : 11) / Drug target genes : 6 - Drug target pathways : 24 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

240. Phenylketonuria


Clinical trials : 182 / Drugs : 144 - (DrugBank : 12) / Drug target genes : 3 - Drug target pathways : 5 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries