79. Homozygous familial hypercholesterolemia Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 525 / Drugs : 330 - (DrugBank : 49) / Drug target genes : 20 - Drug target pathways : 59
| Other names | Familial hypercholesterolemia;Familial hypercholesterolaemia; | ||
|---|---|---|---|
| Disease group | Metabolic diseases | ||
|
Domestic patients
Med expenses recipients, FY2024 (corrected) (in Japanese) |
488 patients Age distribution
|
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| Clinical research form (in Japanese) MHLW Intractable Diseases, FY2026 (in Japanese) | Overview, diagnostic criteria, etc. (pdf), Clinical research form (pdf) | ||
| Specific pediatric chronic diseases, Japan (in Japanese) | 8-12-130. Familial hypercholesterolaemia | ||
| Sub-diseases (Clinical research forms may not be available for all sub-diseases.) | - | ||
