Ataluren
( DrugBank: Ataluren / KEGG DRUG: Ataluren )
6 diseases
ID | Disease name (Link within this page) | Number of trials |
---|---|---|
19 | Lysosomal storage disease | 2 |
113 | Muscular dystrophy | 55 |
140 | Dorabe syndrome | 1 |
ID | Disease name (Link within this page) | Number of trials |
---|---|---|
246 | Methylmalonic acidemia | 5 |
299 | Cystic fibrosis | 43 |
329 | Aniridia | 2 |
19. Lysosomal storage disease
Clinical trials : 990 / Drugs : 584 - (DrugBank : 126) / Drug target genes : 62 - Drug target pathways : 192
No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
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113. Muscular dystrophy
Clinical trials : 766 / Drugs : 477 - (DrugBank : 119) / Drug target genes : 80 - Drug target pathways : 178
No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
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140. Dorabe syndrome
Clinical trials : 139 / Drugs : 49 - (DrugBank : 17) / Drug target genes : 53 - Drug target pathways : 67
No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
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246. Methylmalonic acidemia
Clinical trials : 28 / Drugs : 25 - (DrugBank : 9) / Drug target genes : 18 - Drug target pathways : 26
No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
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299. Cystic fibrosis
Clinical trials : 1,826 / Drugs : 1,271 - (DrugBank : 246) / Drug target genes : 118 - Drug target pathways : 180
No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
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329. Aniridia
Clinical trials : 3 / Drugs : 2 - (DrugBank : 2) / Drug target gene : 0 - Drug target pathway : 0
No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
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